Two babies have received the first-ever gene therapy for Tay-Sachs disease after over 14 years of development. Tay-Sachs is a severe neurological disease caused by a deficiency in an enzyme called ...

Patients in a Phase I/II clinical trial conducted by UMass Chan Medical School of a dual vector gene therapy for GM2 gangliosidosis, which includes Tay-Sachs and Sandhoff diseases, exhibited a ...

JScreen, an organization that encourages people to undergo testing for genetic diseases, has launched a campaign highlighting families who lost children to Tay-Sachs disease. Tay-Sachs is a rare ...

Tay Sachs is a devastating genetic disease with no known cure. But now, experts are hoping a new push for awareness could help parents down the road.

PASCO COUNTY, Fla. (WFLA) — For parents with children with Tay Sachs disease, there’s often little hope, no treatment, and no cure. It’s a rare and deadly disease that attacks the nerve cells in the ...

In a groundbreaking study, researchers at McMaster University have identified a potential treatment for Sandhoff and Tay-Sachs diseases—two rare, often fatal lysosomal storage disorders that cause ...

NEW YORK, Nov. 09, 2020 (GLOBE NEWSWIRE) -- Axovant Gene Therapies Ltd. (NASDAQ: AXGT), a clinical-stage company developing innovative gene therapies, today announced that the U.S. Food and Drug ...

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Tay-Sachs disease results in the deterioration of the nervous system, usually resulting in death before the patient reaches age 5. It is caused by the absence of an enzyme which breaks down lipids, ...