News

Fashion Glamp on MSN21h
Revolutionary Gene Therapy Restores Hearing for Deaf Children
In a groundbreaking development that could herald a new era in the treatment of inherited deafness, a recent clinical trial ...
IFLScience on MSN1d
World-First Gene Therapy Improves Vision For Man With Rare, Previously Untreatable Form Of Blindness
A man born with Usher syndrome type 1b, a rare genetic disease that causes congenital deafness and progressive blindness, has ...
FDA Chief Says He Wants Gene Therapy Head Prasad to Return
US Food and Drug Administration Commissioner Marty Makary said he’s trying to persuade Vinay Prasad, the agency’s former head ...
GEN - Genetic Engineering and Biotechnology News4d
Gene Therapy Companies Set Sights on Cardiovascular Disease
The primary safety risks associated with gene therapy include immune reactions and off-target effects in unintended organs, ...
Diorasis Therapeutics and Northway Biotech Announce Partnership for the Development and Manufacturing of AAV Gene Therapy for Glaucoma
Leveraging Northway Biotech’s 20+ years of CDMO expertise, Diorasis Therapeutics is advancing AAV gene therapy for glaucoma ...
The American Journal of Managed Care5d
Progress and Challenges With Gene Therapy in Hereditary Hearing Loss
Gene therapy appears to be a promising approach for a subset of genetic deafness, although challenges remain with development ...
Progress in gene therapy offers hope for long-term knee pain relief
For nearly three decades, Mayo Clinic researcher Christopher Evans, Ph.D., has pushed to expand gene therapy beyond its ...
Managed Healthcare Executive1d
Effective Strategies for Clinics Preparing to Implement Gene Therapy Into NMIBC Treatment Workflows
An expert discusses how clinics can successfully implement gene therapy workflows by establishing strong institutional protocols, assigning dedicated clinic coordinators, and using strategies like ...
FDA’s Reversal on Gene Therapy Helps My Son
Parents of boys with Duchenne muscular dystrophy weigh in on drug innovation and medical regulation.
Sarepta shares slide again as drugmaker bows to FDA pressure to pause gene therapy
Sarepta Therapeutics is pausing shipments of its gene therapy for muscular dystrophy following several patient deaths that ...
CBS News6y
Experimental Therapy Gives Children With Genetic Disorders A New Chance ...
Local News Experimental Therapy Gives Children With Genetic Disorders A New Chance At Life March 24, 2019 / 7:09 PM PDT / CBS San Francisco by Juliette Goodrich and Molly McCrea ...
NPR7y
Gene Therapy Shows Promise For A Growing List Of Diseases
The first gene therapy product approved by the Food and Drug Administration (a treatment for a form of leukemia, approved last summer) costs hundreds of thousands of dollars for each infusion.